Date Wed, 04/09/2025 - 12:00 Media Pharmacy April 2025 Edit Implementation Schedule For April 2025 Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Modulators Proposal April 2025 Alyftrek NDFB April 2025 Enzyme Deficiency Select Agents Proposal April 2025 Crenessity NDFB April 2025 Kebilidi Proposal April 2025 Kebilidi NDFB April 2025 Transthyretin Amyloidosis Agents Proposal April 2025 Attruby NDFB April 2025 Agenda RDAC Agenda April 2025 Minutes RDAC Minutes April 2025 Approved Criteria Page Rare Disease Council Meeting Information