Meeting Wed, 04/10/2024 - 12:00 Rare Disease Council Meeting Information

Date
Media
Pharmacy April 2024
Edit Implementation Schedule through August 2024
Adzynma Proposal April 2024
Adzynma (ADAMTS13, recombinant-krhn) NDFB April 2024
Pompe Disease Proposal April 2024
Pombiliti (cipaglucosidase alfa-atga) and Opfolda (miglustat) NDFB April 2024
Gene Therapies for Sickle Cell Disease and Beta-Thalassemia Proposal April 2024
Therapies for Sickle Cell Disease and Beta-Thalassemia Comparison
Casgevy (exagamglogene autotemcel) NDFB April 2024
Lyfgenia (lovotibeglogene autotemcel) NDFB April 2024
Zynteglo (betibeglogene autotemcel) NDFB April 2024
Agenda
RDAC Agenda April 2024
Minutes
RDAC Minutes April 2024 Approved
Criteria
Page
Rare Disease Council Meeting Information