Meeting Wed, 10/09/2024 - 12:00 Rare Disease Council Meeting Information

Date
Media
Pharmacy October 2024
Edit Implementation Schedule through February 2025
Sickle Cell Disease Annual Report October 2024
Sickle Cell Disease Proposal October 2024
Gene Therapies for Sickle Cell Disease and Beta-Thalassemia Proposal October 2024
Bile Salt Proposal October 2024
Iqirvo (elafibranor) NDFB October 2024
Complement Inhibitors Systemic Proposal October 2024
Voydeya (danicopan) NDFB October 2024
Duchenne Muscular Dystrophy Proposal October 2024
Elevidys (delandistrogene moxeparvovec-rokl) NDFB October 2024
Epidermolysis Bullosa Proposal October 2024
Filsuvez (birch triterpenes) NDFB October 2024
Hemophilia Gene Therapy Agents Proposal October 2024
Beqvez (fidanacogene elaparvovec-dzkt) NDFB October 2024
Winrevair Proposal October 2024
Winrevair (sotatercept-csrk) NDFB October 2024
Xolremdi Proposal October 2024
Xolremdi (mavorixafor) NDFB October 2024
Agenda
RDAC Agenda October 2024
Minutes
RDAC Minutes October 2024 Approved
Criteria
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Rare Disease Council Meeting Information